The special drug is also the latest treatment drug, the name of the drug is called 'sodium nosinasone'. This drug is for the treatment of spinal muscular atrophy, a mere 5 ml, the price is nearly 700,000 dollars.
This expensive drug is not meant to be given as a single injection, but has to be injected depending on the child's own condition, and may also have to be used for life. Spinal muscular atrophy is also associated with various complications that can jeopardize health. But without the injection, they may not live past the age of 2.
If you have the disease, in addition to expensive injections, you will have to keep a range of medical equipment at home, such as a ventilator, to aid your child's growth.
Spinal muscular atrophy is a relatively common and rare genetic disorder that is an inherited neuromuscular disease. The incidence of the disease in newborns is about 1/6,000-1/10,000. Children with the disease suffer from loss and degeneration of motor neurons located in the anterior horn of the spinal cord and the lower brainstem, resulting in severe muscle atrophy and weakness, making it difficult to roll over, stomp, or crawl, and eventually losing the ability to walk, as well as respiratory and swallowing disorders.
The price of an expensive drug like sodium nasonex is approved by the government. Because it is developed by a high-end medical team and takes more than a decade to develop, and the drug is quite harsh for storage and transportation. Storage and transportation temperatures need to be maintained at 2-8 degrees Celsius, transportation needs to be in a refrigerated box, and temperature data needs to be uploaded and kept on file during transportation to ensure the effectiveness of the drug.
It is hoped that the medical research and development team will be able to bring the drug to mass production soon. I hope that this drug for spinal muscular atrophy will not be so expensive, so that families of children unfortunate enough to have this disease can afford it.